The Muscular Dystrophy Association (MDA) Clinical & Scientific Conference 2025 took place in Dallas, bringing together the neuromuscular (NMD) disease community and stakeholders, including industry representatives, clinicians, patients/caregivers, and patient advocacy groups (PAGs), to share their perspectives on the latest developments in NMD research.
CRA’s Angela De Martini and Tunahan Kirabali examine a few of the key themes that arose out of the numerous sessions, talks, and new data releases, including:
- Advancing early diagnosis and treatment
- The role of genetic medicines in the management of neuromuscular diseases
- The move towards innovative digital and/or biomarker-based endpoints
- Patient/caregiver perspective
Read the full 2025 MDA Clinical & Scientific Conference Review here.