CRA Insights

2025 MDA Clinical & Scientific Conference Review

April 17, 2025
Stethoscope

The Muscular Dystrophy Association (MDA) Clinical & Scientific Conference 2025 took place in Dallas, bringing together the neuromuscular (NMD) disease community and stakeholders, including industry representatives, clinicians, patients/caregivers, and patient advocacy groups (PAGs), to share their perspectives on the latest developments in NMD research.

CRA’s Angela De Martini and Tunahan Kirabali examine a few of the key themes that arose out of the numerous sessions, talks, and new data releases, including:

  • Advancing early diagnosis and treatment
  • The role of genetic medicines in the management of neuromuscular diseases
  • The move towards innovative digital and/or biomarker-based endpoints
  • Patient/caregiver perspective

Read the full 2025 MDA Clinical & Scientific Conference Review here.

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